Professor of Neurology and Medicine, McCaw Endowed Chair in Muscular Dystrophy, University of Washington, Seattle

Dr. Jeffrey Chamberlain’s lab studies mechanisms leading to the muscular dystrophies, the structure & function of dystrophin (mutated in DMD, among the most common inherited diseases), and approaches to therapy. His group developed miniaturized dystrophin genes that we named “micro-dystrophin” and were also the first to show that AAV vectors could be used for systemic gene delivery to muscle.